Dystrophin Quantification in Preclinical and Clinical Settings

Explore the intricacies of dystrophin quantification in preclinical and clinical settings through this 53-minute webinar presented by Dr. Annemieke Aartsma-Rus, a renowned professor of Translational Genetics. Gain insights into Duchenne muscular dystrophy, its genetic causes, and current therapeutic approaches like exon skipping and gene therapy. Delve into the critical question of sufficient dystrophin levels, learn about measurement techniques in clinical trials, and discover how the ProteinSimple capillary immunoassay is utilized in preclinical studies. Enhance your understanding of rare disease drug development, RNA therapeutics, and the latest advancements in muscular dystrophy research from a leading expert in the field.